Expanded access program (USA only)

At Santhera Pharmaceuticals USA, our mission is focused on developing innovative medicines for orphan and other diseases with high unmet medical need. For investigational drugs, consistent with our mission at Santhera Pharmaceuticals USA, we encourage awareness and consideration of participation in clinical trials.

However, when it is not possible for a patient to participate in a clinical trial and all other available medical options have been exhausted, the patient’s physician may seek special access to one of Santhera’s investigational drugs through compassionate use, which may also be called expanded access or preapproval access.

Our full policy on compassionate use can be viewed here:

Santhera Pharmaceuticals USA’s position on offering compassionate use to investigational medicines